Orphan drugs and rare diseases: current landscape, challenges, and future prospects. International Journal of Pharma and Biosciences, India, v. 17, n. 1, p. 39–48, 2026. DOI: 10.22376/ijpbs.v17i1.164. Disponível em: https://lapinjournals.com/index.php/ijpbs/article/view/164. Acesso em: 9 may. 2026.